Genetic Disorders

FDA Grants Accelerated Approval for First Treatment for Barth Syndrome

Physician’s Briefing

FDA Grants Accelerated Approval for First Treatment for Barth Syndrome

25 Sep 2025

1 min read

Apitegromab Improves Motor Function in Spinal Muscular Atrophy

Physician’s Briefing

Apitegromab Improves Motor Function in Spinal Muscular Atrophy

25 Aug 2025

2 min read

Clinical Briefing Report

clinicalbriefingreport.com